Editor's note: In December 2022, researchers at UCLA restarted a clinical trial to test a potential treatment for children with SCID. Jakob Kamil Guziak has not gotten access to the treatment yet ...

Born without a functioning immune system, Mannat Singh is now a healthy 19-month-old after a stem cell transplant. Read more ...

A drug company abandoned a treatment for ‘bubble boy disease.’ After a 5-year fight, this little girl is about to get it By Elizabeth Cohen and Lauren Mascarenhas , CNN ...

Ten children with an especially rare and hard-to-treat form of "bubble boy" disease are living normal lives after receiving a new gene therapy approach, researchers say. Experts said the findings ...

Also known as “bubble boy” or “bubble baby” disease, the disorder was made famous by the 1976 John Travolta movie, “The Boy in the Plastic Bubble.” Seersha was born in Hawaii, where her father was ...

And she learned that the condition is more commonly known as Bubble Boy Disease, a nod to the most famous child ever born with it. Blanca clicked through news stories and black-and-white photos of ...

Later this spring, a little girl in California who essentially has no immune system will receive a lifesaving treatment for “bubble boy disease” thanks to the persistence of a dogged group of ...

Also known as “bubble boy” or “bubble baby” disease, the disorder was made famous by the 1976 John Travolta movie, “The Boy in the Plastic Bubble.” Seersha was born in Hawaii ...

CALIFORNIA -- Later this spring, a little girl in California who essentially has no immune system will receive a lifesaving treatment for "bubble boy disease" thanks to the persistence of a dogged ...