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Sickle cell anaemia is a permanent disorder that influences the structure and the activity of red blood cells .
Discover how doctors at Johns Hopkins All Children's were able to cure a patient born with sickle cell disease thanks to her ...
Research conducted on mice has identified that the rapid response of a specific type of defense cell is essential for ...
First data on treatment of NPC1 with Trappsol® Cyclo™ (hydroxypropyl-beta-cyclodextrin) in this age group over a period of 48 weeksAt 48 weeks of ...