Achondroplasia is a genetic skeletal condition ... spinal stenosis, and hydrocephalus. It is characterized by limited range of motion at the elbows, macrocephaly, small fingers, and normal ...

This is her second trip to the hospital run by CURE, an American faith-based organization that specializes in treating children like Manjeri’s son who suffer from hydrocephalus. It’s a ...

TransCon CNP is an investigational prodrug of C-type natriuretic peptide (CNP) administered once weekly and designed to treat individuals with achondroplasia by providing continuous exposure of ...

NDA supported by data from three randomized, double-blind, placebo-controlled clinical trials in children with achondroplasia, with up to three years of open-label extension data — MAA in EU ...