News

Ice cream for Alpha-1: Omaha event raises awareness about genetic condition
BIG RED ALPHAS GIVES OUT ICE CREAM AND INFORMATION TODAY IN AN ATTEMPT TO RAISE FUNDS ABOUT AN AWARENESS ABOUT A GENETIC ...
Ice cream for Alpha-1: Omaha event raises awareness, funds for genetic condition
Big Red Alphas gave out ice cream and information on Saturday in an attempt to raise funds and awareness about a genetic condition. Alpha-1 antitrypsin deficiency is a condition that affects the lungs ...
Where WAVE Life Sciences Stands With Analysts
Analysts have recently evaluated WAVE Life Sciences and provided 12-month price targets. The average target is $16.0, ...
BioSpace1mon
AIRNA Presents Data Supporting RNA Editing Approach for Alpha-1 Antitrypsin Deficiency (AATD) at 28th ASGCT Annual Meeting - BioSpace
In a poster presentation entitled “Optimized RESTORE+ oligonucleotides for an efficacious and safe RNA base editing treatment for alpha-1 antitrypsin deficiency,” AIRNA’s rAIR-100 research candidates ...
Yahoo Finance1mon
AIRNA Presents Data Supporting RNA Editing Approach for Alpha-1 Antitrypsin Deficiency (AATD) at 28th ASGCT Annual Meeting - Yahoo Finance
CAMBRIDGE, Mass. &, TÜBINGEN, Germany, May 13, 2025--AIRNA today announced preclinical proof-of-concept data supporting its best-in-class RNA editing strategy for alpha-1 antitrypsin deficiency ...
Morningstar1mon
AIRNA Presents Data Supporting RNA Editing Approach for Alpha-1 Antitrypsin Deficiency (AATD) at 28th ASGCT Annual Meeting - Morningstar
In a poster presentation entitled “Optimized RESTORE+ oligonucleotides for an efficacious and safe RNA base editing treatment for alpha-1 antitrypsin deficiency,” AIRNA’s rAIR-100 research ...
Max Planck Society2mon
Alpha-1 antitrypsin deficiency: What protects the one – and not the other?
To the point. Hereditary disease alpha-1-antitrypsin deficiency: Researchers have discovered why some patients remain healthy despite a genetic defect, while others develop severe liver fibrosis Deep ...
PipelineReview.com3mon
AIRNA Raises Oversubscribed $155 Million Series B Financing to Fund Phase 1/2 Clinical Trial for Alpha-1 Antitrypsin Deficiency and Future Pipeline
AIRNA expected to file clinical trial application for Alpha-1 antitrypsin deficiency (AATD) RNA editing product candidate (AIR-001) with potential best-in-class profile in 2H 2025. ... AIRNA ...
Morningstar3mon
AIRNA Raises Oversubscribed $155 Million Series B Financing to Fund Phase 1/2 Clinical Trial for Alpha-1 Antitrypsin Deficiency and Future Pipeline - Morningstar
AIRNA’s lead program has the potential to be a best-in-class therapeutic for alpha-1 antitrypsin deficiency (AATD). AIRNA has headquarters in Cambridge, MA, with research operations in Tübingen ...
casereports.bmj3mon
Detection of nocturnal hypoxaemia leading to a diagnosis of COPD and PiMZ alpha-1 antitrypsin deficiency
Alpha-1 antitrypsin deficiency (AATD) is underdiagnosed, with a significant gap between documented cases and estimated prevalence. ... The gene responsible, SERPINA1, is found on chromosome 14, ...
Taiwan News3mon
KRRO-110 Receives Orphan Drug Designation from U.S. FDA for Alpha-1 Antitrypsin Deficiency | Taiwan News | Mar. 14, 2025 20:00 - 台湾新闻
CAMBRIDGE, Mass., March 14, 2025 (GLOBE NEWSWIRE) -- Korro Bio, Inc. (Korro) (Nasdaq: KRRO), a clinical-stage biopharmaceutical company focused on developing a new class of genetic medicines based on ...