Shares in Wave Life Sciences rose by 74% after it reported clinical data with a pioneering RNA-editing therapy for alpha-1 antitrypsin deficiency (AATD).

A gene-editing delivery system developed by UT Southwestern Medical Center researchers simultaneously targeted the liver and ...

A high-level overview of BioMarin Pharmaceutical Inc. (BMRN) stock. View (BMRN) real-time stock price, chart, news, analysis, analyst reviews and more.

A slew of pharma mergers and acquisitions in the first month of 2024 has continued with a $2.2 billion play by Sanofi for Inhibrx and its clinical-stage drug candidate for alpha-1 antitrypsin ...

CRISPR Therapeutics CRSP and Intellia Therapeutics NTLA are leading developers of therapies that utilize the Nobel ...

BACKGROUND--Previous estimates of the survival times of patients with alpha 1-antitrypsin deficiency have been based on selected patients. METHODS--The survival times of 397 patients with severe alpha ...

Tensions rise as Taiwan restricts Chinese tech exports, sparking Beijing's retaliation. Discover key impacts on tech, markets, and global relations.

Liver problems: Rinvoq may increase liver enzyme levels, ... (RA) that can lead to folate deficiency. Discover the symptoms, how to treat it, and more. READ MORE.

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