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Discover how doctors at Johns Hopkins All Children's were able to cure a patient born with sickle cell disease thanks to her ...
Sickle cell anaemia is a permanent disorder that influences the structure and the activity of red blood cells .
Vertex Pharmaceuticals (Nasdaq: VRTX) announced today a reimbursement agreement with the Italian Medicines Agency (AIFA) for ...
Research conducted on mice has identified that the rapid response of a specific type of defense cell is essential for ...
A Minnesota woman has filed a lawsuit that alleges her surgeon removed her kidney, and not her spleen, in 2022, leaving her with significant health issues According to the lawsuit documents, Wendy ...
First data on treatment of NPC1 with Trappsol® Cyclo™ (hydroxypropyl-beta-cyclodextrin) in this age group over a period of 48 weeksAt 48 weeks of ...