“It gets lost in the system just like a lot of other things get lost in the system,” he said. “But it shouldn’t.” Patterson’s granddaughter is 5 years old, the same age as the child ...

Background Spinal muscular atrophy type 1 (SMA 1) typically presents before 6 months of age with progressive muscle weakness, bulbar dysfunction and respiratory failure. Nusinersun is the first ...

Unlock the secrets to building stronger, more defined pecs. This guide covers the best exercises and a deep dive into the anatomy of your chest muscles for optimal growth.

Body type refers to the shape of bodies. The three main types are endomorph, mesomorph, and ectomorph. Learn about the traits ...

Four-year data show preservation of cardiac function, including LVEFSkeletal muscle disease progression continues to slow with extended treatment (PUL v2.0)Deramiocel’s long-term safety profile ...

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today provided a safety ...

The PPMD Annual Conference is the largest international event focused on advancing research, clinical trials, and standards of care for Duchenne and Becker muscular dystrophies. Capricor's ...

SAN DIEGO, June 20, 2025 (GLOBE NEWSWIRE) -- Capricor Therapeutics (NASDAQ: CAPR), a biotechnology company developing transformative cell and exosome-based therapeutics for rare diseases, today ...

About HOPE-2 Open Label Extension (OLE) Study HOPE-2 was a randomized, double-blind, placebo-controlled Phase 2 study of Deramiocel in boys and young men with Duchenne Muscular Dystrophy (DMD).