Muscular dystrophy, as a category, is quite diverse. There's dozens of disorders that we would put under that umbrella, so it's hard to be specific about what we would do for everybody.

So this would be in some areas of the world now considering newborn screening as a potential option for identifying neonates who are affected with muscular dystrophy or having good vigilance on ...

Children with a rare form of muscular dystrophy have been promised access to a groundbreaking drug after the Sunday Mail highlighted their plight. Around 30 boys could have their lives extended by ...

The contrarian strips away what's necessary to discover the core drivers of value. Allison C. Ullrich, founder and CEO of Potentiate OS, is one of the few forward-thinking individuals who embody ...

Sznajder says about 95% of children with autism have an additional symptom, and that there is a comorbidity between autism and more than 100 other diseases, including myotonic dystrophy.

Just a few weeks after Avidity Biosciences made a stir with new data on its experimental therapy for Duchenne muscular dystrophy, the biotech has closed a public offering that raised an impressive ...

Gilbert Ullrich, who has lamented the "dark storm clouds that will bring about new challenges," was supportive of Mr Trump’s election and his commitment to protect it as an American industry. Ullrich ...

I’d like to share another small part of the movement that has been particularly significant to the muscular dystrophy (MD) community: the passage of the Muscular Dystrophy Community Assistance, ...

Italfarmaco’s oral HDAC inhibitor givinostat has been approved in the US as a treatment for Duchenne muscular dystrophy (DMD), becoming the first non-steroidal option for patients with all ...

Patients with myotonic dystrophy have smaller hearts, and lower systolic and diastolic blood pressures and pulse rates. They have impaired autonomic reflexes, measured by orthostatic, Valsalva ...

DALLAS—Facioscapulohumeral muscular dystrophy (FSHD) and limb-girdle muscular dystrophy (LGMD) are both extremely rare diseases, with a US prevalence of 4 per 100,000 inhabitants for FSHD and 2-10 per ...