CRISPR Therapeutics CRSP and Intellia Therapeutics NTLA are leading developers of therapies that utilize the Nobel ...

A gene-editing delivery system developed by UT Southwestern Medical Center researchers simultaneously targeted the liver and ...

A gene-editing delivery system developed by UT Southwestern Medical Center researchers simultaneously targeted the liver and ...

The ZZ genotype of alpha-1 antitrypsin deficiency (AATD) is associated with COPD regardless of smoking. Heterozygous MZ-AATD is recognised as a moderate deficiency state, increasing the risk of COPD ...

Alpha-1 Antitrypsin Deficiency Market Research 2025-2035, Competitive Analysis of Grifols, CSL Behring, Takeda Pharmaceuticals, LFB Biotechnologies, GlaxoSmithKline, AstraZeneca, Merck, Pfizer - ...

The global alpha-1 antitrypsin deficiency (AATD) market is expanding, driven by advances in diagnosis, treatment, and growing awareness. Key players like Grifols, CSL Behring, and Pfizer lead ...

The major toxicity with acetaminophen is to the liver, and it is dose-related. At 4 grams a day, there is often an elevation of liver enzymes. (The CMP does contain liver tests that are commonly ...

Beam Therapeutics Announces U.S. FDA Orphan Drug Designation Granted to BEAM-302 for the Treatment of Alpha-1 Antitrypsin Deficiency (AATD) Published May 29, 2025 4:01pm EDT ...